Adenine base editing with engineered virus-like particles rescues the CFTR mutation G542X in patient-derived intestinal organoids
- Lucia Nicosia
- , Iwona Pranke
- , Roberta V. Latorre
- , Joss B. Murray
- , Lisa Lonetti
- , Kader Cavusoglu-Doran
- , Elise Dreano
- , James P. Costello
- , Michael Carroll
- , Paola Melotti
- , Claudio Sorio
- , Isabelle Sermet-Gaudelus
- , Martina F. Scallan
- , Patrick T. Harrison
- Université Paris Descartes-Sorbonne-Paris Cité
- Université Paris Cité
- University of Verona
- Azienda Ospedaliera Universitaria Integrata di Verona
- European Reference Network
- Cincinnati Children's Hospital Medical Center
Research output: Contribution to journal › Article › peer-review