CRISPR-based gene editing enables FOXP3 gene repair in IPEX patient cells
- M. Goodwin
- , E. Lee
- , U. Lakshmanan
- , S. Shipp
- , L. Froessl
- , F. Barzaghi
- , L. Passerini
- , M. Narula
- , A. Sheikali
- , C. M. Lee
- , G. Bao
- , C. S. Bauer
- , H. K. Miller
- , M. Garcia-Lloret
- , M. J. Butte
- , A. Bertaina
- , A. Shah
- , M. Pavel-Dinu
- , A. Hendel
- , M. Porteus
- Stanford University
- San Raffaele Telethon Institute for Gene Therapy
- Rice University
- Phoenix Children's Hospital
- University of California at Los Angeles
- Bar-Ilan University
Research output: Contribution to journal › Article › peer-review