In Vivo Genome Editing at the Albumin Locus Corrects Two New Mouse Models of Methylmalonic Acidemia (MMA) Caused by Methylmalonyl-CoA Mutase Deficiency (Mmut)

TY - JOUR

T1 - In Vivo Genome Editing at the Albumin Locus Corrects Two New Mouse Models of Methylmalonic Acidemia (MMA) Caused by Methylmalonyl-CoA Mutase Deficiency (Mmut)

AU - Schneller, Jessica L.

AU - Lee, Ciaran M.

AU - Li, Ang

AU - Cradick, Thomas J.

AU - Chandler, Randy J.

AU - Hurley, Ayrea E.

AU - Lagor, William R.

AU - Bao, Gang

AU - Venditti, Charles P.

PY - 2020

Y1 - 2020

UR - https://publons.com/wos-op/publon/41768986/

M3 - Article

SN - 1525-0016

JO - Molecular Therapy

JF - Molecular Therapy

ER -