Optogenetic modeling of human neuromuscular circuits in Duchenne muscular dystrophy with CRISPR and pharmacological corrections
- Amaia Paredes-Redondo
- , Peter Harley
- , Eleni Maniati
- , David Ryan
- , Sandra Louzada
- , Jinhong Meng
- , Anna Kowala
- , Beiyuan Fu
- , Fengtang Yang
- , Pentao Liu
- , Silvia Marino
- , Olivier Pourquié
- , Francesco Muntoni
- , Jun Wang
- , Ivo Lieberam
- , Yung Yao Lin
- Queen Mary University of London
- King's College London
- Wellcome Trust Sanger Institute
- University College London
- The University of Hong Kong
- Harvard University
- Great Ormond Street Hospital for Children NHS Foundation Trust
- Universidade de Trás-os-Montes e Alto Douro
- University of Lisbon
Research output: Contribution to journal › Article › peer-review