Targeted replacement of full-length CFTR in human airway stem cells by CRISPR-Cas9 for pan-mutation correction in the endogenous locus
- Sriram Vaidyanathan
- , Ron Baik
- , Lu Chen
- , Dawn T. Bravo
- , Carlos J. Suarez
- , Shayda M. Abazari
- , Ameen A. Salahudeen
- , Amanda M. Dudek
- , Christopher A. Teran
- , Timothy H. Davis
- , Ciaran M. Lee
- , Gang Bao
- , Scott H. Randell
- , Steven E. Artandi
- , Jeffrey J. Wine
- , Calvin J. Kuo
- , Tushar J. Desai
- , Jayakar V. Nayak
- , Zachary M. Sellers
- , Matthew H. Porteus
- Stanford University
- Department of Otolaryngology–Head and Neck Surgery
- Rice University
- University of North Carolina at Chapel Hill
Research output: Contribution to journal › Article › peer-review